Multidisciplinary team meetings in treatment of spinal muscular atrophy adult patients: a real-life observatory for innovative treatments

Salort-Campana E, Sole G, Magot A, Tard C, Noury JB, Behin A, De La Cruz E, Boyer F, Lefeuvre C, Masingue M, Debergé L, Finet A, Brison M, Spinazzi M, Pégat A, Sacconi S, Malfatti E, Choumert A, Bellance R, Bedat-Millet AL, Féasson L, Vuillerot C, Jacquin-Piques A, Michaud M, Pereon Y, Stojkovic T, Laforet P, Attarian S, Cintas P

Orphanet journal of rare diseases