Support our Foundation of Myology project
PTA17333 Avaglucosidase
A French multicentre, phase 4, open-label extension study of long-term safety and efficacy in patients with Pompe disease who previously took part in development studies.
Support our Foundation of Myology project
A French multicentre, phase 4, open-label extension study of long-term safety and efficacy in patients with Pompe disease who previously took part in development studies.