Save the date! 4th Neuromuscular Translational School, Nov. 21st-25th in Leiden, TheNetherlands

The upcoming 4th Neuromuscular Translational School (under auspices of EURO-NMD and TREAT-NMD) will be held from November 21st- November 25th in Leiden (The Netherlands).

Organized by Annemieke Aartsma-Rus (Leiden University Medical Center, LUMC, the Netherlands & John Walton Muscular Dystrophy Research Center, Newcastle University, UK), Teresinha Evangelista (Institut de Myologie, Group Hospitalier Pitié-Salpêtrière, Paris, France), Silvere van der Maarel (Leiden University Medical Center, LUMC, the Netherlands) and Andoni Urtizberea (Institut de Myologie, Paris, France), the 4th Neuromuscular Translational School aims to facilitate the clinical development of therapies for NMDs.

Objectives:

• Educate clinicians and researchers working in the NMD field on aspects relevant for translational therapy development:

o   Bench to bedside research
o   Regulatory system
o   Clinical trials
o   Outcome measures
o   Patient communication
o   Registries and biobanks
o   Biomarkers and -omics

• Outline and showcase how networks like EURO-NMD and TREAT-NMDTreat-NMD est un réseau européen d’excellence dans le domaine dans maladies neuromusculaires, dont le but est de créer l’infrastructure qui garantit que les recherches les plus prometteuses atteignent les patients le plus rapidement possible. Depuis sa création en janvier 2007, Treat-NMD s’est concentré sur le développement d’outils (registres de patients…) dont l’industrie, les cliniciens et les scientifiques ont besoin pour amener de nouvelles approches thérapeutiques à la clinique, et sur l’établissement des meilleures pratiques de soins des personnes atteintes de maladie neuromusculaire dans le monde. facilitate therapy development

o   Standards of care
o   Clinical trial tools
o   Outcome measure development
o   Interaction with stakeholders

Target audience:

• MDs
• PhD/Postdoc researchers
• Others working in translational research
• Preferably in the NMD field, but in either case working in the RD field
• Aim for 16 participants (definitely no more than 20 – or we lose the interactivity)
• Industry delegates

Access the 4th Neuromuscular Translational School programme

 

Applications via the ERN Euro-NMD website