Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors

Gapinske M, Winter J, Swami D, Gapinske L, Woods WS, Shirguppe S, Miskalis A, Busza A, Joulani D, Kao CJ, Kostan K, Bigot A, Bashir R, Perez-Pinera P

Molecular therapy. Nucleic acids