SUNFISH Parts 1 and 2: 4-year Efficacy and Safety Data of Risdiplam in Types 2 and 3 Spinal Muscular Atrophy (SMA) (S34.009)

Servais L, Oskoui M, Day J, Deconinck N, Mazzone E, Nascimento A, Saito K, Vuillerot C, Baranello G, Boespflug-Tanguy O, Goemans N, Kirschner J, Kostera-Pruszczyk A, Braid J, Papp G, Gorni K, Martin C, Scalco R, Yeung WY, Mercuri E

Neurology