Poster 24 : Safety and tolerability of Eteplirsen in patients 6–48 Months old with DMD amenable to exon 51 skipping: an open-label extension study

Mercuri E, Seferian A, Deconinck N, Orogun L, Ni X, Zhang W, Drummond K, Sehinovych I, Muntoni F

Neuromuscular disorders : NMD