Poster 149 : Delayed pulmonary progression in Golodirsen-treated patients with Duchenne muscular dystrophy vs mutation-matched external controls

Iff J, Tuttle E, Liu Y, Wei F, Done N, Servais L, Seferian A, Straub V, Guglieri M, Mercuri E, Muntoni F, Sekou G

Neuromuscular disorders : NMD