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Loss of ambulation in SMA III at the time of disease-modifying treatments: an international study.
Coratti G, Bovis F, Franchino V, Montes J, Sansone VA, Dunaway Young S, Cutrì C, Pasternak A, Pera MC, Pane M, Glanzman A, Pegoraro E, Duong T, Sogus E, Sframeli M, Messina S, Cavalcante E, Scoto MC, D’Amico A, Rodriguez-Torres R, Mongini T, Maggi L, Coccia M, Filosto M, Zuccarino R, Masson R, Ricci G, Bruno C, Ruggiero L, Vacchiano V, D’Errico E, Verriello L, Nigro V, Scarpini G, Garibaldi M, Turri M, Ticci C, Berardinelli A, Agosto C, Ricci F, Zolkipli-Cunningham Z, Darras BT, Day J, Hirano M, Muntoni F, Finkel RS, Mercuri E
Journal of neurology, neurosurgery, and psychiatry