Functional benefit of CRISPR-Cas9-induced allele deletion for RYR1 dominant mutation

Beaufils M, Melka M, Brocard J, Benoit C, Debbah N, Mamchaoui K, Romero NB, Dalmas-Laurent AF, Quijano-Roy S, Fauré J, Rendu J, Marty I

Molecular therapy. Nucleic acids