Disease Exacerbation in 3D MYOtissues Derived From Duchenne Muscular Dystrophy iPSC Reveals Muscle Strength Loss and Enables Gene Therapy Screening

Palmieri L, Pili L, Jaber A, Moula M, Hong AV, El-Khoury R, Brochier G, Bigot A, Israeli D, Richard I, Albini S