- PTA17333 Avaglucosidase: A French multicenter Phase 4 open label extension study of long -term safety and efficacy in patients with Pompe disease who previously participated in avalglucosidase development studies in France.
- French Pompe disease register
- International Pompe Disease Register
Acronym |
PTA17333 Avaglucosidase |
French Pompe disease register |
International Pompe disease register |
| Intervention | Avalglucosidase alpha | – | – |
| Principal investigator | Anthony Behin | Pascal Laforet | Pascal Laforet |
| Sponsor | Sanofi | Institute of Myology | Sanofi |
| Study status | Active | Active | Active |
| Recruitment status | Completed | ||
| Population | Adult | Adult | Adult |
| + infos on clinicaltrials.gov | |||
| Contact | essais-adultes@institut-myologie.org |
