AADC Deficiency

  • AADCAware: An International, Real-World, Observational Registry Of The Natural History Of Subjects Diagnosed With Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency

 

Acronym

AADCAware

Principal investigator Claudia Ravelli
Sponsor PTC Therapeutics
Study status In preparation
Recruitment status In preparation
Population Child