AADC Deficiency

  • PTC-AADC-MA-406: An Two Part, International, Real-World, Observational Registry Of Participants Diagnosed With Aromatic L-Amino Acid Decarboxylase Deficiency (AADC) With or Without Treatment With Eladocagene Exuparvovec

 

Acronym

PTC-AADC-MA-406

Principal investigator Claudia Ravelli
Sponsor PTC Therapeutics
Study status Ongoing
Recruitment status Ongoing
Population Child