Cell immortalisation

MyoLine platform

With the development of many innovative therapeutic approaches for genetic diseases, targeting DNA, RNA or proteins, muscle cells isolated from patients, known as myoblasts, are an ideal in vitro model for evaluating these approaches in neuromuscular diseases. These cells have several advantages: they are easy to work with, they reduce the number of animal experiments, and they carry the patient’s exact mutation in their own genetic background.

These in vitro approaches do have limits, however: human somatic cells have a limited proliferation capacity, governed by the mitotic clock, and reach replicative senescence after a set number of divisions. This proliferation limit is reached even earlier in degenerative diseases. The MyoLine platform neutralises the replicative senescence of human muscle cells using a double transduction with lentiviral vectors, thereby creating immortal human cell lines.

More than 200 human myoblast lines

Since it was set up in 2007, the MyoLine human cell immortalisation platform has generated more than 200 human myoblast lines isolated from patients with more than 36 different neuromuscular diseases (DMD, LGMD, FSHD, SMA…). As access to muscle biopsies can be limited for some diseases, it has also developed the immortalisation of skin fibroblasts. These immortalised fibroblasts are then transduced with an inducible MyoD transcription factor, and these myoconverted cells form myotubes and express muscle markers in the same way as muscle cells.

The loss of muscle mass in patients with neuromuscular diseases is often accompanied by its replacement with fibrous and/or fatty tissue. In recent years, research in this field has focused on the role played by fibro-adipogenic progenitors (FAPs), because of their ability to differentiate into adipocytes or fibroblastic cells.
To support this research, MyoLine is currently developing FAP models isolated from a range of muscular dystrophies.

Where the consent signed by the donor allows it, the cell lines can also be used under material transfer agreements for the development of therapeutic tools by private partners.

Team members

Anne Bigot, research project manager, platform manager
Mona Bensalah, research engineer (IR)
Kamel Mamchaoui, research engineer (IR)
Vincent Mouly, emeritus research director
Jessica Ohana, study engineer (IE)