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Poster 149 : Delayed pulmonary progression in Golodirsen-treated patients with Duchenne muscular dystrophy vs mutation-matched external controls
Iff J, Tuttle E, Liu Y, Wei F, Done N, Servais L, Seferian A, Straub V, Guglieri M, Mercuri E, Muntoni F, Sekou G
Neuromuscular disorders : NMD