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Poster 281 : Quality of life in adults with dysferlinopathy: international clinical outcome study of dysferlinopathy
Hilsden H, James M, Dressman H, Day J, Mendell J, Torron R, Harms M, Pestronk A, Vissing J, Desai U, Yoshimura M, Shin J, Mozaffar T, Stojkovic T, Pegoraro E, Raivas J, Olive M, Paradas C, Straub V, Mayhew A
Neuromuscular disorders : NMD