The most bothersome symptoms in neuromuscular diseases: the ERN EURO NMD Survey

Mancuso M, Colitta A, Lavorato M, van den Bergh P, Kirschner J, Kornblum C, Maggi L, Lamy F, Lochmuller H, Nordstrøm M, Malfatti E, Ferlini A, Pareyson D, Silani V, Kleopa KA, de Visser M, Atalaia A, Evangelista T

Orphanet journal of rare diseases