Becker Muscular Dystrophy is due to mutations in the dystrophin gene located on chromosome X, inducing severedefects in dystrophin protein. This abnormal dystrophin weakens muscular cells.
Clinical trial ongoing at the Institute:
- Becker Coeur: Cardiac involvement in Becker’s myopathy: evaluation of prognostic markers
- EDG-5506 BMD: A Phase 2 Randomized, Double-blind, Placebo-controlled Study to Evaluate the Effect of EDG-5506 on Safety, Biomarkers, Pharmacokinetics, and Functional Measures in Adults and Adolescents with Becker Muscular Dystrophy
Type of research |
RBM-HPS |
EDG-5506 BMD |
| Intervention | – | EDG-5506 |
| Principal investigator | Karim Wahbi | T. Stojkovic |
| Sponsor | AIM | Edgewise Th |
| Study status | Ongoing | Active |
| Recruitment status | Closed | Closed |
| Population | Adult | Terminé |
| Contact | karim.wahbi@psl.aphp.fr | Adulte |
| + infos on clinicaltrials.gov | + info on clinicaltrials.gov |
