Poster 227 MANATEE: GYM329 (RO7204239) in combination with Risdiplam treatment in patients with spinal muscular atrophy (SMA)

Duong T, Darras B, Morrow J, Muntoni F, Servais L, Rabbia M, Gerber M, Kletzl H, Gaki E, Fletcher S, Scalco R, Wagner K, Mercuri E

Neuromuscular disorders : NMD