Poster 230 : Safety update: Risdiplam clinical trial program for spinal muscular atrophy (SMA)

Baranello G, Chiriboga C, Servais L, Darras B, Day J, Deconinck N, Farrar M, Finkel R, Bertini E, Kirschner J, Rasson M, Mazurkiewicz-Beldzinska M, Vlodavets D, Bader-Weder S, Gorni K, Jaber B, Yeung WY, Papp G, Scalco R, Mercuri E

Neuromuscular disorders : NMD