CRISPR-Cas9-Mediated Upregulation of Utrophin Ameliorates Duchenne Muscular Dystrophy

Ralu M, Guiraud S, Dastidar S, Galbiati P, Sadaoui E, Mazed F, Amor F, De Cian A, Richard I, Mamchaoui K, Ronzitti G, Tedesco FS, Amendola M

Molecular therapy : the journal of the American Society of Gene Therapy