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A toolkit for new facioscapulohumeral muscular dystrophy trial sites
Kools J, Korngut L, Petrillo Ballantyne J, Roozen I, de Haas R, Hill A, Evangelista T, Sansone VA, Roxburgh R, Lochmuller H, Statland J, Johnson NE, Voermans N
Journal of Neuromuscular Diseases