Martino, A. T., Basner-Tschakarjan, E., Markusic, D. M., Finn, J. D., Hinderer, C., Zhou, S., Ostrov, D. A., Srivastava, A., Ertl, H. C., Terhorst, C., High, K. A., Mingozzi, F., Herzog, R. W. :
Engineered AAV vector minimizes in vivo targeting of transduced hepatocytes by capsid-specific CD8+ T cells
Blood, 2013 ; 121 (12) : 2224-33
Publications (1184)
Cavalcante, P., Cufi, P., Mantegazza, R., Berrih-Aknin, S., Bernasconi, P., Le Panse, R. :
Etiology of myasthenia gravis: Innate immunity signature in pathological thymus Autoimmun Rev, 2013 ; 12 (9) : 863-74
Etiology of myasthenia gravis: Innate immunity signature in pathological thymus Autoimmun Rev, 2013 ; 12 (9) : 863-74
Benveniste, O. :
Gene therapy, an ongoing revolution Blood, 2012 ; 119 (13) : 2973-2974
Gene therapy, an ongoing revolution Blood, 2012 ; 119 (13) : 2973-2974
Furling, D. :
Misregulation of alternative splicing and microRNA processing in DM1 pathogenesis Rinsho Shinkeigaku, 2012 ; 52 (11) : 1018-22
Misregulation of alternative splicing and microRNA processing in DM1 pathogenesis Rinsho Shinkeigaku, 2012 ; 52 (11) : 1018-22
Malfatti, E., Birouk, N., Romero, N. B., Piraud, M., Petit, F. M., Hogrel, J. Y., Laforet, P. :
Juvenile-onset permanent weakness in muscle phosphofructokinase deficiency J Neurol Sci, 2012 ; 316 (1-2) : 173-177
Juvenile-onset permanent weakness in muscle phosphofructokinase deficiency J Neurol Sci, 2012 ; 316 (1-2) : 173-177
Stojkovic, T., Benyaou, R. :
Les syndromes scapulopéroniers La Lettre du Neurologue, 2012 ; 16 (1) : 16-22
Les syndromes scapulopéroniers La Lettre du Neurologue, 2012 ; 16 (1) : 16-22
Boudreau, E., Labib, S., Bertrand, A. T., Decostre, V., Bolongo, P. M., Sylvius, N., Bonne, G., Tesson, F. :
Lamin a/c mutants disturb sumo1 localization and sumoylation in vitro and in vivo PLoS ONE, 2012 ; 7 (9) : e45918
Lamin a/c mutants disturb sumo1 localization and sumoylation in vitro and in vivo PLoS ONE, 2012 ; 7 (9) : e45918
Hage Hassan, R., Hainault, I., Vilquin, J. T., Samama, C., Lasnier, F., Ferre, P., Foufelle, F., Hajduch, E. :
Endoplasmic reticulum stress does not mediate palmitate-induced insulin resistance in mouse and human muscle cells Diabetologia, 2012 ; 55 (1) : 204-214
Endoplasmic reticulum stress does not mediate palmitate-induced insulin resistance in mouse and human muscle cells Diabetologia, 2012 ; 55 (1) : 204-214
Muchir, A., Reilly, S. A., Wu, W., Iwata, S., Homma, S., Bonne, G., Worman, H. J. :
Treatment with selumetinib preserves cardiac function and improves survival in cardiomyopathy caused by mutation in the lamin A/C gene Cardiovasc Res, 2012 ; 93 (2) : 311-319
Treatment with selumetinib preserves cardiac function and improves survival in cardiomyopathy caused by mutation in the lamin A/C gene Cardiovasc Res, 2012 ; 93 (2) : 311-319
Wahbi, K., Duboc, D. :
Arrhythmia Management in Myotonic Dystrophy Type 1. Reply JAMA, 2012 ; 308 (4) : 338
Arrhythmia Management in Myotonic Dystrophy Type 1. Reply JAMA, 2012 ; 308 (4) : 338
