Clinical Trials in Focus: Innovations and Patient Perspectives in Rare Diseases
Friday 28 February 2025 – 12:00 PM – 1:30 PM (CET)
Alexandre Mejat (AFM-Téléthon) • The Need for Innovation in Clinical Trial Methodologies for Muscular Disorders
Edoardo Malfatti (AP-HP) • Overview of Outcome Mesures in Neuromuscular Disorder Clinical Trials
Gérald Perret (Généthon) • Lessons Learned from a Decade of Duchenne Muscular Dystrophy (DMD)
> Platform: Online (link provided upon registration)
> Register here
Hosted by the Dreams (Horizon Europe) consortium
