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Breaking news
- 21 November 2025 More is now known about the pathophysiology of myotubularin
- 21 November 2025 ERN EURO-NMD webinar, 26 Nov.: Dr. Adela Della Marina (Germany)
- 20 November 2025 ERN EURO-NMD webinar, 26 Nov.: Prof. Dr. med. Andreas Meisel (Germany)
- 20 November 2025 The lysosome, a potential therapeutic target in DMD
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