{"id":1489,"date":"2019-01-18T15:32:12","date_gmt":"2019-01-18T13:32:12","guid":{"rendered":"https:\/\/www.institut-myologie.org\/imotion\/?p=1489"},"modified":"2019-01-18T15:54:44","modified_gmt":"2019-01-18T13:54:44","slug":"deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion","status":"publish","type":"post","link":"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/","title":{"rendered":"DMD : les essais WAVE-OLE et Anti-myostatin viennent de d\u00e9marrer \u00e0 I-Motion"},"content":{"rendered":"<p>La <strong>phase OLE de Wave\u00a0<\/strong>vient de d\u00e9buter. Cet essai d\u2019extension en ouvert et multicentrique vise \u00e0 \u00e9valuer le WVE-210201 chez des gar\u00e7ons atteints de la <a href=\"https:\/\/www.afm-telethon.fr\/dystrophie-musculaire-duchenne-1251\" target=\"_blank\" rel=\"noopener\">dystrophie musculaire de Duchenne\u00a0<\/a>pr\u00e9c\u00e9demment inclus dans WVE-DMDX51-001, qui \u00e9taient \u00e9ligibles au saut d\u2019exon 51. Le premier patient de I-Motion a \u00e9t\u00e9 screen\u00e9 le 7 janvier.<\/p>\n<p>Toujours dans la dystrophie musculaire de Duchenne, le premier patient de l\u2019institut a \u00e9t\u00e9 screen\u00e9 juste avant les f\u00eates dans l\u2019\u00e9tude <strong>Anti-myostatin<\/strong>. Aussi appel\u00e9e Spitfire, cette \u00e9tude de phase 2\/3, en double aveugle et contr\u00f4l\u00e9e contre placebo, a pour but d\u2019\u00e9valuer l\u2019efficacit\u00e9, la s\u00e9curit\u00e9 et la tol\u00e9rance de BMS-986089 administr\u00e9 \u00e0 des gar\u00e7ons de 6 \u00e0 11 ans ambulants, atteints de DMD. Cette mol\u00e9cule\u00a0pourrait favoriser la croissance musculaire en inhibant la myostatine, une prot\u00e9ine qui limite cette croissance.<\/p>\n<p>&nbsp;<\/p>\n<blockquote><p>En savoir plus sur l\u2019essai WAVE-OLE <a href=\"https:\/\/www.institut-myologie.org\/essais\/essais-en-cours\/myopathie-de-duchenne\/dmd-essais-de-pharmacologie-1\/\">ici<\/a><br \/>\nEn savoir plus sur l\u2019essai Anti-Myostatine <a href=\"https:\/\/www.institut-myologie.org\/essais\/essais-en-cours\/myopathie-de-duchenne\/dmd-essais-de-pharmacologie-4\/\">ici <\/a>et <a href=\"https:\/\/www.afm-telethon.fr\/myopathie-duchenne-essai-ro7239361-bms-986089-123646\" target=\"_blank\" rel=\"noopener\">l\u00e0<\/a><\/p><\/blockquote>\n","protected":false},"excerpt":{"rendered":"<p>La phase OLE de Wave\u00a0vient de d\u00e9buter. Cet essai d\u2019extension en ouvert et multicentrique vise \u00e0 \u00e9valuer le WVE-210201 chez des gar\u00e7ons atteints de la dystrophie musculaire de Duchenne\u00a0pr\u00e9c\u00e9demment inclus dans WVE-DMDX51-001, qui \u00e9taient \u00e9ligibles au saut d\u2019exon 51. Le premier patient de I-Motion a \u00e9t\u00e9 screen\u00e9 le 7 janvier. Toujours dans la dystrophie musculaire &hellip; <a href=\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\">Continued<\/a><\/p>\n","protected":false},"author":3,"featured_media":0,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":""},"categories":[5],"tags":[],"class_list":["post-1489","post","type-post","status-publish","format-standard","hentry","category-actualites-cliniques"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.1.1 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>DMD : les essais WAVE-OLE et Anti-myostatin viennent de d\u00e9marrer \u00e0 I-Motion - I-Motion<\/title>\n<meta name=\"description\" content=\"Les essais dans la dystrophie musculaire de Duchenne Anti-myostatin et WAVE-OLE\u00a0viennent de d\u00e9marrer \u00e0 l&#039;Institut I-Motion.\" \/>\n<meta name=\"robots\" content=\"index, nofollow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\" \/>\n<meta property=\"og:locale\" content=\"fr_FR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"DMD : les essais WAVE-OLE et Anti-myostatin viennent de d\u00e9marrer \u00e0 I-Motion - I-Motion\" \/>\n<meta property=\"og:description\" content=\"Les essais dans la dystrophie musculaire de Duchenne Anti-myostatin et WAVE-OLE\u00a0viennent de d\u00e9marrer \u00e0 l&#039;Institut I-Motion.\" \/>\n<meta property=\"og:url\" content=\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\" \/>\n<meta property=\"og:site_name\" content=\"I-Motion\" \/>\n<meta property=\"article:published_time\" content=\"2019-01-18T13:32:12+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2019-01-18T13:54:44+00:00\" \/>\n<meta name=\"author\" content=\"Anne Berthomier\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:label1\" content=\"\u00c9crit par\" \/>\n\t<meta name=\"twitter:data1\" content=\"Anne Berthomier\" \/>\n\t<meta name=\"twitter:label2\" content=\"Dur\u00e9e de lecture estim\u00e9e\" \/>\n\t<meta name=\"twitter:data2\" content=\"1 minute\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\/\/schema.org\",\"@graph\":[{\"@type\":\"Article\",\"@id\":\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/#article\",\"isPartOf\":{\"@id\":\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\"},\"author\":{\"name\":\"Anne Berthomier\",\"@id\":\"https:\/\/www.institut-myologie.org\/imotion\/#\/schema\/person\/ecf0b87715a026a200491fe2d7649def\"},\"headline\":\"DMD : les essais WAVE-OLE et Anti-myostatin viennent de d\u00e9marrer \u00e0 I-Motion\",\"datePublished\":\"2019-01-18T13:32:12+00:00\",\"dateModified\":\"2019-01-18T13:54:44+00:00\",\"mainEntityOfPage\":{\"@id\":\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\"},\"wordCount\":173,\"publisher\":{\"@id\":\"https:\/\/www.institut-myologie.org\/imotion\/#organization\"},\"articleSection\":[\"Actualit\u00e9s cliniques\"],\"inLanguage\":\"fr-FR\"},{\"@type\":\"WebPage\",\"@id\":\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\",\"url\":\"https:\/\/www.institut-myologie.org\/imotion\/2019\/01\/18\/deux-essais-portant-sur-la-dmd-viennent-de-demarrer-motion\/\",\"name\":\"DMD : les essais WAVE-OLE et Anti-myostatin viennent de d\u00e9marrer \u00e0 I-Motion - 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