Spinal Muscular Atrophies – 2

  • FIREFISH: A two part seamless multicenter study to investigate the safety, tolerability, pharmacokinetics, pharmacodynamics and efficacy of RO7034067 in infants with spinal muscular atrophy type 1
  • SUNFISH: A two-part seamless, multi-center randomized, placebo-controlled, doubleblind study to investigate the safety, tolerabilty, pharmacokinetics, pharmacodynamics and efficacy of RO7034067 in type 2 and 3 spinal muscular atrophy patients

 

 

Acronym

SUNFISH

FIREFISH

Study type
RBM RBM
Trial type International multicenter trial International multicenter trial
Intervention RO70344067 vs Placebo RO70344067
Principal investigator Laurent Servais Laurent Servais
Sponsor Roche Roche
Fundings Roche Roche
Study status Ongoing Ongoing
Recruitment status Ongoing Ongoing
Population Adult / Child Child
Contact l.servais@institut-myologie.org l.servais@institut-myologie.org
+ infos on clinicaltrials.gov + infos on clinicaltrials.gov