Institut de Myologie Autour des malades : pôles de recherche, d'enseignement et d'expertise sur le muscle Access to extranet

Therapeutic protocols

PTC : extension study open-label in DMD patients with stop mutation (international study)

Investigator
Pr T . Voit
Sponsor PTC
CCPPRB
Yes
Patient numbers
Total
At the Institute of Myology
 
165
4
Projected dates
Beginning
Ending
 
July 2009
July 2011
Financing
PTC
Outcome measures 6 MWT; EK scale; biology; cognition,
Update : October 2009